List view / Grid view

Gene Therapy

 

Gene Therapy is the introduction of normal genes into cells in place of missing or defective ones in order to correct genetic disorders.

news

New gene variant identified in ALS provides treatment hope

17 May 2017 | By

A new study shows that a variant in UBQLN4 gene has been associated with Lou Gehrig's disease, or amyotrophic lateral sclerosis (ALS). The study also describes how this gene variant disrupts a cellular process that drives motor neuron development. This new insight opens the door to potential treatment targets for…