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Complete DNA sequence of the X chromosome revealed
Researchers capitalised on novel sequencing technologies to produce the first end-to-end DNA sequence of the X chromosome.
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CRISPR: kick-starting the revolution in drug discovery
Gene editing using the CRISPR system has been established as the most powerful tool in the search for new drugs and is now being exploited for therapeutic purposes. Here, Pushpanathan Muthuirulan discusses the promises and wider opportunities of using CRISPR technology to open up the possibility of large-scale screening of…
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Groundbreaking gene therapy trial set to cure haemophilia
A cure for haemophilia is one step closer, following results of a gene therapy trial led by the NHS in London.
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Microcapsules to enhance the efficiency of genome-editing
Researchers have found that polymer and hybrid silica-coated microcapsules are efficient in genome-editing...
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Apitope raises €12 million in Series B funding
29 September 2015 | By Victoria White
The funds will enable Apitope to progress the clinical development of its innovative pipeline which includes therapies for Factor VIII intolerance in Haemophilia A patients...
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FDA Grants Orphan Status for ATX-F8-117 for the treatment of haemophilia A patients in the US
9 June 2015 | By Victoria White
Apitope’s product candidate ATX-F8-117 has been granted Orphan Drug Status by the FDA for the treatment of patients with haemophilia A in the US...
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Alnylam and collaborators publish preclinical results on ALN-AT3 for the treatment of haemophilia
14 April 2015 | By Victoria White
Preclinical results on ALN-AT3, an investigational RNAi therapeutic targeting AT for the treatment of haemophilia and RBD, have been published...
