news New muscular dystrophy treatment shows promise in pre-clinical trials 30 June 2020 | By Victoria Rees (Drug Target Review) A group of researchers has used locked nucleic acid gapmer antisense oligonucleotides to treat facioscapulohumeral muscular dystrophy in cells and mice.
news Using CRISPR-Cas9 to identify new gene drug targets 26 March 2020 | By Victoria Rees (Drug Target Review) Researchers have used CRISPR-Cas9 to screen the genome for possible targets that could be used in potential treatments for muscular dystrophy.