beta-thalassemia

hand holding a section of a DNA strand above the remaining strand with forceps - idea of gene editing

news

TALEN is a more efficient gene editing tool for tightly packed DNA, finds study

28 January 2021 | By Hannah Balfour (Drug Target Review)

TALEN was shown to be almost five times more efficient than CRISPR-Cas9 at locating and editing genes in heterochromatin.

news

Experimental treatment for sickle cell disease success

20 June 2019 | By Victoria Rees (Drug Target Review)

Researchers announce positive pre-clinical results for two sickle cell disease treatment strategies.

news

PNA gene editing technique cures beta-thalassemia in utero

10 July 2018 | By Dr Zara Kassam (Drug Target Review)

Researchers have for the first time used a gene editing technique to successfully cure a genetic condition in a mouse model...

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beta-thalassemia

TALEN is a more efficient gene editing tool for tightly packed DNA, finds study

Experimental treatment for sickle cell disease success

PNA gene editing technique cures beta-thalassemia in utero